FDA approves 1st treatment for rare disorders in children, adults
The FDA approved Cholbam, a cholic acid, for children and adults with bile acid synthesis disorders and peroxisomal disorders, according to a press release from the FDA. After the manufacturer was granted a rare pediatric disease priority review voucher, the FDA announced the approval of Cholbam as an oral treatment for adults and children at least three weeks old, according to the release.
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